By Holly Lebowitz Rossi
Updated: August 10, 2018

A drug traditionally used to prevent the rejection of organ transplants is giving new hope to parents of children with progeria, a rare genetic disorder that causes premature aging and death usually before age 12.  Scientists at Children's Hospital and the National Institutes of Health are currently planning a large-scale clinical trial to see whether the drug rapamycin, or a similar medication, might help remove the damaging protein progerin from patients' cells.

According to a report in The Boston Globe:

If successful, the clinical trial could offer hope to those afflicted with the rare disease, which affects an estimated 1 in 4-8 million newborns.  It might also shed light on ways to repurpose existing drugs to fight other aging and neurological diseases like Parkinson's.

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